Subgroup data show crinecerfont helps children with CAH reduce steroid use while maintaining or improving androstenedione levels across diverse patient groups. On May 8, 2025, Neurocrine Biosciences ...

In this video interview, Jenna Marcovitz, MA, MT-BC, CCLS, RMT, provides insight to music therapy and how it can benefit a wide range of pediatric patients. In this video interview, Jenna Marcovitz, ...

In this interview, Suzanne Hollander, MS, RD, LDN, discusses the importance of collaborative care in PKU and the impact of a new potential treatment. As the phenylketonuria (PKU) community anticipates ...

Respiratory syncytial virus (RSV) illness is an extremely common cause of hospitalization in children in the United States and globally. An estimated 90% of children will be infected by 2 years of age ...

Josue did not speak any English when he first walked into my office. He was with his new foster mother for his initial foster screen: a lively 7-year-old from Puerto Rico, jumping all over the room ...

Zhang Meng shares how advancements in technology have helped prevent early cavities in childhood, and how to counsel your young patients on good oral health. Technology is king these days, starting at ...

FDA, HHS announces plan to enhance quality, safety of domestic infant formula ...

A review of the clinical potential of PTC Therapeutics' sepiapterin as a novel treatment for phenylketonuria (PKU). Phenylketonuria (PKU), a rare genetic disorder that affects the body’s ability to ...

Even before the change in national leadership, access to adolescent gender-affirming care was becoming more difficult, with many barriers faced by these at-risk patients. Gender-affirming care (GAC) ...

On physical examination, the patient appeared to be in significant respiratory distress. Her oxygen saturation was 96% on high-flow nasal cannula. An 18-day-old female presented to the Emergency ...

In a May 7, 2025 announcement, Infinant Health stated that its investigational drug candidate INF108 received both orphan drug and rare pediatric disease designations for the prevention of necrotizing ...

Prescriptions for the epinephrine nasal spray are now available for patients aged 4 years and up who weigh 33 to < 66 lbs. On May 7, 2025, ARS Pharmaceuticals announced that epinephrine nasal spray ...